Hereditary Angioedema (HAE)

Current Studies

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Study 331-201

Recruiting

Study 331-201: A Phase 1/2, Open-Label, Dose-Escalation Study to Determine the Safety, Tolerability, and Efficacy of BMN 331, an Adeno-Associated Virus (AAV) Vector-Mediated Gene Transfer of Human SERPING1, in Subjects with Hereditary Angioedema (HAE) due to Human C1 Esterase Inhibitor (C1-INH) Deficiency

• Indication

  Hereditary Angioedema (HAE)

• Investigational therapeutic

  BMN 331

• Study Type

  Phase 1/2

• Goal

  This open label, two-part study aims to establish the safety, tolerability, and efficacy of BMN 331

• Status

  This study is currently recruiting participants

• Study Website

  http://haegenestudy.com/

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